Gene Therapy: A Transformative Shift in Rare Disease Treatment Video Gene Therapy: A Transformative Shift in Rare Disease Treatment After decades of promise, gene therapy is finally starting to deliver on its potential—especially for…Danielle Pillsbury2025 年 2 月 26 日
CMS Cell and Gene Therapy (CGT) Access Model Explained: The Most Significant Drug Pricing Legislation You’ve Never Heard Of Blog CMS 细胞与基因治疗(CGT)准入模式详解:你从未听说过的最重要的药品定价立法 2024 年 12 月 13 日 The Centers for Medicare & Medicaid Services (CMS) is piloting a program…Danielle Pillsbury2024 年 12 月 13 日
Model-Informed Approaches and Innovative Clinical Trial Design for Adeno-Associated Viral Vector-Based Gene Therapy Product Development: A White Paper Publication Model-Informed Approaches and Innovative Clinical Trial Design for Adeno-Associated Viral Vector-Based Gene Therapy Product Development: A White Paper The promise of viral vector-based gene therapy (GT) as a transformative paradigm for treating severely…Danielle Pillsbury2023 年 6 月 14 日
The Promises and Pitfalls of Gene Therapy for Rare Diseases On-Demand Webinar 基因疗法治疗罕见病的希望与陷阱 The state of gene therapy faces much uncertainty as recent regulatory and clinical setbacks have…Jim Gallagher2021 年 4 月 29 日
Getting Gene Therapies to Patients Blog 为患者提供基因疗法 This blog discusses the challenges that drug developers face in getting patients access to cell…Ulrich Neumann2021 年 2 月 16 日
Early Value Assessment in Gene Therapy Clinical Trial Design Case Study 基因治疗临床试验设计中的早期价值评估 A global biotechnology company engineering precision genetic medicine for rare diseases was in need of…Jim Gallagher2021 年 2 月 12 日
Dose Optimization using the Gene Therapy Virtual Twin Platform Blog 利用基因治疗虚拟双胞胎平台优化剂量 This blog explains how using the Gene Therapy Virtual Twin™ Platform can help optimize dosing…Piet van der Graaf2021 年 1 月 22 日