2025 ISPE 年会

Challenge(s):

• Limited data availability due to rarity of condition
• Locating small and dispersed patient populations
• Incomplete data sources that lack all necessary variables to study, e.g., outcomes and resource utlization but not quality of life or clinical measures.

解决方案: Certara’s Real-World Evidence team use an innovative approach to link retrospective chart review studies as well a rare disease registry to the SNDS French National Health Claims Database to obtain a better understanding of rare genetic disorder progression and identy unmet needs.