Quantitative Systems Pharmacology-Based Digital Twins Approach Supplements Clinical Trial Data for Enzyme Replacement Therapies in Pompe Disease Publication 基于定量系统药理学的数字双胞胎方法补充了庞贝氏症酶替代疗法的临床试验数据 Pompe disease is a rare, progressive neuromuscular disease caused by deficient lysosomal glycogen degradation, and…Danielle Pillsbury2024 年 12 月 4 日